Stem cells are on the forefront of the fight against rare pediatric diseases. Experts discuss current therapies and future hopes while a father shares his experience getting treatment for his son.

Moderated by Mort Cowan, MD, UC San Francisco
Pawash Priyank: Patient Perspective
Diana Farmer, MD, FACS, FRCS, UC Davis: Making Miracles Come To Life Through Stem Cells
Rosa Bacchetta, MD, Stanford University: Towards a cure for IPEX: engineered-Treg replacement or stem cell gene editing Recorded on 09/15/2020. (#36346)